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Real-world data utilisation case studies concerning drug-induced liver injury in paediatric rare diseases

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Society, Date, Venue:
The 46th Annual Meeting of the Japanese Society for Clinical Pharmacology (5 December 2025), presented at,
5 December 2025, Tokyo

Title:
Real-world data utilisation case studies concerning drug-induced liver injury in paediatric rare diseases

Speakers:
Masayoshi Nakakuni1), Kosuke Nakano1), Ayano Inui2), Seiji Mitsui1), Naoko Deguchi1), Seiko Miyazaki3)

Institution:
1) Network Promotion Unit, Department of Multicenter Collaboration, Clinical Research Center, National Center for
Child Health and Development
2) Saiseikai Yokohama Eastern Hospital Paediatric Hepatology and Gastroenterology Department
3) Pharmacoepidemiology Unit, Center for Social and Pharmacy Education and Research,
Teikyo Heisei University School of Pharmacy